Investors map · Worldwide

Who invests in rare disease

37 investors have backed two or more of the 70 rare disease startups worldwide on our map, in rounds we track. Grouped by kind, each ranked by how many of these companies it has backed; the most active has backed 7.

37investors on the map
3kinds of investor
5AM Venturesbacked the most (4)
VC firmsmost common kind

Segment by segment

VC firms

21 investors

  1. 5AM VenturesVC firmUnited States4 backed
  2. SanofiInvestment firmFrance4 backed
  3. Novo HoldingsVC firmDenmark4 backed
  4. Samsara BioCapitalVC firmUnited States4 backed
  5. KurmaPartnersVC firmFrance3 backed
  6. Alexandria Real Estate EquitiesVC firmUnited States3 backed
  7. FidelityVC firmUnited States3 backed
  8. Atlas VentureVC firmUnited States2 backed

Private equity and asset managers

13 investors

  1. OrbiMedPrivate equityUnited States7 backed
  2. Cormorant Asset ManagementPrivate equityUnited States4 backed
  3. RA Capital ManagementPrivate equityUnited States4 backed
  4. BCBain Capital Life SciencesPrivate equityUnited States3 backed
  5. Foresite CapitalPrivate equityUnited States3 backed
  6. Perceptive AdvisorsAsset managerUnited States3 backed
  7. EurazeoPrivate equityFrance2 backed
  8. Idinvest PartnersPrivate equityFrance2 backed

Corporate investors

3 investors

  1. PfizerCorporate investorUnited States2 backed
  2. Novartis Venture FundCorporate investorSwitzerland2 backed
  3. Sanofi VenturesCorporate investorUnited States2 backed

How this map is made. Every investor here has backed two or more startups on our rare disease map, in rounds we track. Grouped by the kind of investor, each ranked by how many of these companies it has backed. Rebuilt nightly; updated 15 November 2026.

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