Top list · Worldwide
Gene therapy startups worldwide
81 gene therapy startups worldwide have raised money in rounds we track. These are the 50 that have raised the most, $4.8B between them, with the United States the most common home.
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FerGeneFerGene is an new Gene therapy, spin off Ferring Pharmaceuticals.FerGene is an new Gene therapy, spin off Ferring Pharmaceuticals.
Founded 2019Saint-prex$570Mlast round Nov 2019 - 2
Ori BiotechOri Biotech is a biotechnology company based in London and Philadelphia, focused on cell and gene therapy (CGT) manufacturing technology.Ori Biotech is a biotechnology company based in London and Philadelphia, focused on cell and gene therapy (CGT) manufacturing technology.
Founded 2015London, United Kingdom$435Mlast round Jun 2022 - 3
Passage BioPassage Bio is a fully integrated gene therapy company developing therapies for the treatment of monogenic central nervous system diseases.Passage Bio is a fully integrated gene therapy company developing therapies for the treatment of monogenic central nervous system diseases.
Founded 2018United States$380Mlast round Jan 2021 - 4Heyuan BiotechnologyHeyuan Biotechnology is a biotechnology company focusing on the field of gene therapy services.
Heyuan Biotechnology is a biotechnology company focusing on the field of gene therapy services.
Founded 2013Shanghai$300Mlast round Jun 2020 - 5
Shape TherapeuticsA biotechnology company developing RNA technologies to shape the future of gene therapyA biotechnology company developing RNA technologies to shape the future of gene therapy
Founded 2018Seattle, United States$260Mlast round Jul 2026 - 6
Beacon TherapeuticsBeacon Therapeutics is a clinical-stage ophthalmic gene therapy company founded in 2023, dedicated to saving and restoring vision for patients with retinal diseBeacon Therapeutics is a clinical-stage ophthalmic gene therapy company founded in 2023, dedicated to saving and restoring vision for patients with retinal dise
Founded 2023Alachua, United States$247Mlast round Jan 2026 - 7
Voyager TherapeuticsVoyager Therapeutics is a biotechnology company specializing in gene therapy and neurology.Voyager Therapeutics is a biotechnology company specializing in gene therapy and neurology.
Founded 2013Cambridge, United States$205Mlast round Jan 2024 - 8
Frontera TherapeuticsFrontera Therapeutics is an AAV gene therapy company that focuses on rAAV therapies for the global market.
Frontera Therapeutics is an AAV gene therapy company that focuses on rAAV therapies for the global market.
Founded 2019Bedford, United States$160Mlast round Jun 2022 - 9
LEXEO TherapeuticsLEXEO Therapeutics utilizes gene therapy to treat genetically defined cardiovascular and central nervous system diseases.LEXEO Therapeutics utilizes gene therapy to treat genetically defined cardiovascular and central nervous system diseases.
Founded 2018New York, United States$154Mlast round Oct 2025 - 10
Atsena TherapeuticsAtsena Therapeutics is a clinical-stage gene therapy company based in Durham, North Carolina, focused on developing treatments for inherited retinal diseases (IAtsena Therapeutics is a clinical-stage gene therapy company based in Durham, North Carolina, focused on developing treatments for inherited retinal diseases (I
Founded 2019Durham, United States$150Mlast round Apr 2025 - 11
VectorYVectorY Therapeutics is an Amsterdam-based biotechnology company founded in August 2020.VectorY Therapeutics is an Amsterdam-based biotechnology company founded in August 2020.
Founded 2020Amsterdam, Netherlands$138Mlast round Nov 2023 - 12Gyroscope TherapeuticsGyroscope Therapeutics is a clinical-stage gene therapy company focused on developing therapies and treating diseases of the eye.
Gyroscope Therapeutics is a clinical-stage gene therapy company focused on developing therapies and treating diseases of the eye.
Founded 2016Stevenage, United Kingdom$118Mlast round Nov 2021 - 13
SalioGen TherapeuticsSalioGen Therapeutics was a genetic medicine company founded in 2019 or 2020 and based in Lexington/Cambridge, Massachusetts.SalioGen Therapeutics was a genetic medicine company founded in 2019 or 2020 and based in Lexington/Cambridge, Massachusetts.
Founded 2020Lexington, United States$115Mlast round Jan 2022 - 14
Dyno TherapeuticsDyno Therapeutics is a biotechnology company based in Watertown, Massachusetts, founded in 2018.Dyno Therapeutics is a biotechnology company based in Watertown, Massachusetts, founded in 2018.
Founded 2018Watertown, United States$100Mlast round May 2021 - 15
Neurophth TherapeuticsNeurophth Therapeutics is a leading clinical-stage gene therapy company based in Wuhan, China, with additional subsidiaries in Shanghai, Suzhou, and San Diego, USA.Neurophth Therapeutics is a leading clinical-stage gene therapy company based in Wuhan, China, with additional subsidiaries in Shanghai, Suzhou, and San Diego, USA.
Founded 2016Wu Han Shi, China$97Mlast round Aug 2023 - 16
Vivet TherapeuticsVivet Therapeutics is a biotechnology company developing gene therapy treatments for orphan diseases.Vivet Therapeutics is a biotechnology company developing gene therapy treatments for orphan diseases.
Founded 2016Paris, France$96Mlast round Feb 2024 - 17
Forge BiologicsForge Biologics is a hybrid gene therapy contract manufacturing and therapeutic development company based in Grove City, Ohio.Forge Biologics is a hybrid gene therapy contract manufacturing and therapeutic development company based in Grove City, Ohio.
Founded 2020Columbus, United States$90Mlast round Sept 2022 - 18
Ring TherapeuticsRing Therapeutics is a biotechnology company based in Cambridge, Massachusetts, founded in 2017 by Flagship Pioneering.Ring Therapeutics is a biotechnology company based in Cambridge, Massachusetts, founded in 2017 by Flagship Pioneering.
Founded 2017Cambridge, United States$87Mlast round Mar 2023 - 19
GenSight BiologicsGenSight Biologics develops gene therapy-based treatments for retinal degenerative diseases.GenSight Biologics develops gene therapy-based treatments for retinal degenerative diseases.
Founded 2012Paris, France$80Mlast round Mar 2026 - 20
XyloCor TherapeuticsXyloCor Therapeutics is a bio-pharmaceutical company intended to develop gene therapy for people with advanced coronary artery disease.XyloCor Therapeutics is a bio-pharmaceutical company intended to develop gene therapy for people with advanced coronary artery disease.
Founded 2013King of Prussia, United States$68Mlast round Feb 2025 - 21
Apertura Gene TherapyApertura Gene Therapy is a biotechnology company focused on developing advanced gene therapies for rare and genetic diseases.Apertura Gene Therapy is a biotechnology company focused on developing advanced gene therapies for rare and genetic diseases.
Founded 2021New York, United Kingdom$67Mlast round Apr 2022 - 22
Cyllene TherapeuticsEG 427, operating under the name Cyllene Therapeutics, is a biotechnology company based in Paris.EG 427, operating under the name Cyllene Therapeutics, is a biotechnology company based in Paris.
Founded 2019Paris, France$66Mlast round Jul 2026 - 23
Akamis BioAkamis Bio is a clinical-stage oncology company based in Cambridge, Massachusetts, dedicated to improving treatment for colorectal cancer and other solid tumors.Akamis Bio is a clinical-stage oncology company based in Cambridge, Massachusetts, dedicated to improving treatment for colorectal cancer and other solid tumors.
Founded 2010Cambridge, United Kingdom$60Mlast round Dec 2024 - 24
Myonexus TherapeuticsMyonexus Therapeutics is a clinical stage gene therapy company developing first ever treatments for Limb-girdle muscular dystrophy types.Myonexus Therapeutics is a clinical stage gene therapy company developing first ever treatments for Limb-girdle muscular dystrophy types.
Founded 2017Columbus$60Mlast round May 2018 - 25IxakaIxaka is a private cell and gene therapy company with a focus on the natural power of the body to cure disease.
Ixaka is a private cell and gene therapy company with a focus on the natural power of the body to cure disease.
Founded 2015London$54Mlast round Jan 2021 - 26
Scout BioScout Bi is a biotechnology company that specializes in veterinary, animal health, and gene therapy.Scout Bi is a biotechnology company that specializes in veterinary, animal health, and gene therapy.
Founded 2016Philadelphia, United States$53Mlast round Oct 2021 - 27
GenespireGenespire is a biotechnology company based in Milan, Italy, focused on developing innovative gene therapies for severe genetic diseases.Genespire is a biotechnology company based in Milan, Italy, focused on developing innovative gene therapies for severe genetic diseases.
Founded 2020Milan, Italy$52Mlast round Sept 2024 - 28
NewBiologixNewBiologix is a biotechnology and technology innovation company based in Epalinges, Switzerland, founded in 2022-2023.NewBiologix is a biotechnology and technology innovation company based in Epalinges, Switzerland, founded in 2022-2023.
Founded 2023Epalinges, Switzerland$50Mlast round May 2023 - 29
Spot BiosystemsSpot Biosystems is building the next generation of non-viral gene therapy with an extracellular vesicle (EV) delivery platform.Spot Biosystems is building the next generation of non-viral gene therapy with an extracellular vesicle (EV) delivery platform.
Founded 2018Palo Alto, United States$40Mlast round Jun 2026 - 30
Apic BioApic Bio, Inc.Apic Bio, Inc.
Founded 2017Cambridge, United States$40Mlast round Jan 2019 - 31
Opus GeneticsOpus Genetics is a gene therapy company for ultra-rare blinding conditions.Opus Genetics is a gene therapy company for ultra-rare blinding conditions.
Founded 2004Farmington Hills, United States$35Mlast round Apr 2026 - 32
Advanced Medicine PartnersAdvanced Medicine Partners is a biotechnology company focused on process development, manufacturing, analytical development, and testing for advanced therapy prAdvanced Medicine Partners is a biotechnology company focused on process development, manufacturing, analytical development, and testing for advanced therapy pr
Founded 2023Cary, United States$32Mlast round Jun 2024 - 33
CoJourneyCoJourney is a global Contract Development and Manufacturing Organization (CDMO) focused on cell and gene therapy.CoJourney is a global Contract Development and Manufacturing Organization (CDMO) focused on cell and gene therapy.
Founded 2021Philadelphia, United States$30Mlast round Jun 2023 - 34
Genenta ScienceGenenta Science is a biotechnology company that develops gene transfer therapy for the treatment of cancer tumors.Genenta Science is a biotechnology company that develops gene transfer therapy for the treatment of cancer tumors.
Founded 2014Milano, Italy$30Mlast round Oct 2025 - 35
Newracle GeneticsNewracle Genetics is a bio venture company that develops gene therapy products for neurological diseases.Newracle Genetics is a bio venture company that develops gene therapy products for neurological diseases.
Founded 2018Seoul$27Mlast round Jun 2021 - 36
Mana.bioMana.bio is an AI-based biotechnology startup founded in 2021, focused on enhancing targeted gene therapy delivery.Mana.bio is an AI-based biotechnology startup founded in 2021, focused on enhancing targeted gene therapy delivery.
Founded 2021San Francisco, United States$20Mlast round Sept 2025 - 37
Celosia TherapeuticsA biotechnology company that uses gene therapy to treat neurodegenerative diseases.A biotechnology company that uses gene therapy to treat neurodegenerative diseases.
Founded 2022Sydney, Australia$17Mlast round Nov 2024 - 38
TozaroTozaro Limited is a UK-based biotechnology research company located in Colworth Park, Bedfordshire.Tozaro Limited is a UK-based biotechnology research company located in Colworth Park, Bedfordshire.
Founded 2015Bedford, United Kingdom$16Mlast round Feb 2026 - 39
StrideBioStrideBio is a gene therapy company that develops genetic medicines with curative potential for patients with devastating conditions.StrideBio is a gene therapy company that develops genetic medicines with curative potential for patients with devastating conditions.
Founded 2015United States$16Mlast round Jun 2018 - 40
NeuExcell TherapeuticsNeuExcell Therapeutics is an early-stage gene therapy company focused on neurodegenerative diseases and central nervous system injuries.NeuExcell Therapeutics is an early-stage gene therapy company focused on neurodegenerative diseases and central nervous system injuries.
Founded 2016King of Prussia, United States$15Mlast round May 2023 - 41
CelltrioCelltrio is a life sciences company based in Fremont, California, specializing in automation solutions for cell culturing, biobanking, and cell and gene therapy.Celltrio is a life sciences company based in Fremont, California, specializing in automation solutions for cell culturing, biobanking, and cell and gene therapy.
Founded 2018Fremont, United States$15Mlast round Jun 2025 - 42
CalimmuneCalimmune is a clinical-stage gene therapy company.Calimmune is a clinical-stage gene therapy company.
Founded 2006United States$15Mlast round May 2015 - 43Sino-BiocanSino-Biocan focuses on the research and development of domestic tools in the field of cell and gene therapy.
Sino-Biocan focuses on the research and development of domestic tools in the field of cell and gene therapy.
Founded 2013Beijing$14Mlast round Mar 2024 - 44
Tongli Haiyuan BiotechnologyTongli Haiyuan Biotechnology focuses on the R&D and production of GMP-grade core raw material reagents for upstream cell and gene therapy.Tongli Haiyuan Biotechnology focuses on the R&D and production of GMP-grade core raw material reagents for upstream cell and gene therapy.
Founded 2011China$13Mlast round Mar 2023 - 45
ImmunoVecImmunoVec develops gene therapy treatments to cure terminal genetic diseases of the immune system.ImmunoVec develops gene therapy treatments to cure terminal genetic diseases of the immune system.
Founded 2019Santa Monica, United States$13Mlast round Jul 2026 - 46AAVLifeWildlife engages in developing gene therapy for the treatment of rare diseases.
Wildlife engages in developing gene therapy for the treatment of rare diseases.
Founded 2014Paris, France$12Mlast round Apr 2014 - 47
SomagenetixSomagenetix is a Swiss biotech company based in Zurich, specializing in gene therapy for phagocyte-related disorders and inherited genetic diseases.Somagenetix is a Swiss biotech company based in Zurich, specializing in gene therapy for phagocyte-related disorders and inherited genetic diseases.
Founded -Zuerich, Switzerland$12Mlast round Oct 2024 - 48
GenascenceClinical-stage biotechnology company developing life-changing gene therapy products for musculoskeletal diseasesClinical-stage biotechnology company developing life-changing gene therapy products for musculoskeletal diseases
Founded 2017Palo Alto, United States$12Mlast round Feb 2023 - 49
AutolomousAutolomous is an biotechnology company engaged in manufacturing pragmatic digital solutions for cell and gene therapy.Autolomous is an biotechnology company engaged in manufacturing pragmatic digital solutions for cell and gene therapy.
Founded 2019London, United Kingdom$11Mlast round Mar 2025 - 50
CardionCardion is a biopharmaceutical company that develops cardiovascular gene therapy products.Cardion is a biopharmaceutical company that develops cardiovascular gene therapy products.
Founded 1996Germany$11Mlast round Sept 2002
London, United Kingdom
United States
Amsterdam, Netherlands
Wu Han Shi, China
Paris, France
Milan, Italy
Epalinges, Switzerland
Sydney, Australia
GermanyCompanies whose own description names this theme, ranked by the total they have raised in rounds we hold. Nobody pays to be on a list.
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