# Top 50 Gene Therapy Startups Worldwide by Funding (2026) > The 50 best-funded gene therapy startups worldwide, ranked by total funding raised: $4.8B combined. With founding year, headquarters and each company's rounds. Source: https://millionrounds.com/top-lists/gene-therapy-startups (Millionrounds; every figure on the page links to its filing or article) - 1 [**FerGene** FerGene is an new Gene therapy, spin off Ferring Pharmaceuticals.](https://millionrounds.com/company/fergene) FerGene is an new Gene therapy, spin off Ferring Pharmaceuticals. *Founded* 2019 Saint-prex **$570M** last round Nov 2019 - 2 [**Ori Biotech** Ori Biotech is a biotechnology company based in London and Philadelphia, focused on cell and gene therapy (CGT) manufacturing technology.](https://millionrounds.com/company/ori-biotech) Ori Biotech is a biotechnology company based in London and Philadelphia, focused on cell and gene therapy (CGT) manufacturing technology. *Founded* 2015 London, United Kingdom **$435M** last round Jun 2022 - 3 [**Passage Bio** Passage Bio is a fully integrated gene therapy company developing therapies for the treatment of monogenic central nervous system diseases.](https://millionrounds.com/company/passage-bio) Passage Bio is a fully integrated gene therapy company developing therapies for the treatment of monogenic central nervous system diseases. *Founded* 2018 United States **$380M** last round Jan 2021 - 4 [**Heyuan Biotechnology** Heyuan Biotechnology is a biotechnology company focusing on the field of gene therapy services.](https://millionrounds.com/company/heyuan-biotechnology) Heyuan Biotechnology is a biotechnology company focusing on the field of gene therapy services. *Founded* 2013 Shanghai **$300M** last round Jun 2020 - 5 [**Shape Therapeutics** A biotechnology company developing RNA technologies to shape the future of gene therapy](https://millionrounds.com/company/shape-therapeutics) A biotechnology company developing RNA technologies to shape the future of gene therapy *Founded* 2018 Seattle, United States **$260M** last round Jul 2026 - 6 [**Beacon Therapeutics** Beacon Therapeutics is a clinical-stage ophthalmic gene therapy company founded in 2023, dedicated to saving and restoring vision for patients with retinal dise](https://millionrounds.com/company/beacon-therapeutics) Beacon Therapeutics is a clinical-stage ophthalmic gene therapy company founded in 2023, dedicated to saving and restoring vision for patients with retinal dise *Founded* 2023 Alachua, United States **$247M** last round Jan 2026 - 7 [**Voyager Therapeutics** Voyager Therapeutics is a biotechnology company specializing in gene therapy and neurology.](https://millionrounds.com/company/voyager-therapeutics) Voyager Therapeutics is a biotechnology company specializing in gene therapy and neurology. *Founded* 2013 Cambridge, United States **$205M** last round Jan 2024 - 8 [**Frontera Therapeutics** Frontera Therapeutics is an AAV gene therapy company that focuses on rAAV therapies for the global market.](https://millionrounds.com/company/frontera-therapeutics) Frontera Therapeutics is an AAV gene therapy company that focuses on rAAV therapies for the global market. *Founded* 2019 Bedford, United States **$160M** last round Jun 2022 - 9 [**LEXEO Therapeutics** LEXEO Therapeutics utilizes gene therapy to treat genetically defined cardiovascular and central nervous system diseases.](https://millionrounds.com/company/lexeo-therapeutics) LEXEO Therapeutics utilizes gene therapy to treat genetically defined cardiovascular and central nervous system diseases. *Founded* 2018 New York, United States **$154M** last round Oct 2025 - 10 [**Atsena Therapeutics** Atsena Therapeutics is a clinical-stage gene therapy company based in Durham, North Carolina, focused on developing treatments for inherited retinal diseases (I](https://millionrounds.com/company/atsena-therapeutics) Atsena Therapeutics is a clinical-stage gene therapy company based in Durham, North Carolina, focused on developing treatments for inherited retinal diseases (I *Founded* 2019 Durham, United States **$150M** last round Apr 2025 - 11 [**VectorY** VectorY Therapeutics is an Amsterdam-based biotechnology company founded in August 2020.](https://millionrounds.com/company/vectory) VectorY Therapeutics is an Amsterdam-based biotechnology company founded in August 2020. *Founded* 2020 Amsterdam, Netherlands **$138M** last round Nov 2023 - 12 [**Gyroscope Therapeutics** Gyroscope Therapeutics is a clinical-stage gene therapy company focused on developing therapies and treating diseases of the eye.](https://millionrounds.com/company/gyroscope-therapeutics) Gyroscope Therapeutics is a clinical-stage gene therapy company focused on developing therapies and treating diseases of the eye. *Founded* 2016 Stevenage, United Kingdom **$118M** last round Nov 2021 - 13 [**SalioGen Therapeutics** SalioGen Therapeutics was a genetic medicine company founded in 2019 or 2020 and based in Lexington/Cambridge, Massachusetts.](https://millionrounds.com/company/saliogen-therapeutics) SalioGen Therapeutics was a genetic medicine company founded in 2019 or 2020 and based in Lexington/Cambridge, Massachusetts. *Founded* 2020 Lexington, United States **$115M** last round Jan 2022 - 14 [**Dyno Therapeutics** Dyno Therapeutics is a biotechnology company based in Watertown, Massachusetts, founded in 2018.](https://millionrounds.com/company/dyno-therapeutics) Dyno Therapeutics is a biotechnology company based in Watertown, Massachusetts, founded in 2018. *Founded* 2018 Watertown, United States **$100M** last round May 2021 - 15 [**Neurophth Therapeutics** Neurophth Therapeutics is a leading clinical-stage gene therapy company based in Wuhan, China, with additional subsidiaries in Shanghai, Suzhou, and San Diego, USA.](https://millionrounds.com/company/neurophth-therapeutics) Neurophth Therapeutics is a leading clinical-stage gene therapy company based in Wuhan, China, with additional subsidiaries in Shanghai, Suzhou, and San Diego, USA. *Founded* 2016 Wu Han Shi, China **$97M** last round Aug 2023 - 16 [**Vivet Therapeutics** Vivet Therapeutics is a biotechnology company developing gene therapy treatments for orphan diseases.](https://millionrounds.com/company/vivet-therapeutics) Vivet Therapeutics is a biotechnology company developing gene therapy treatments for orphan diseases. *Founded* 2016 Paris, France **$96M** last round Feb 2024 - 17 [**Forge Biologics** Forge Biologics is a hybrid gene therapy contract manufacturing and therapeutic development company based in Grove City, Ohio.](https://millionrounds.com/company/forge-biologics) Forge Biologics is a hybrid gene therapy contract manufacturing and therapeutic development company based in Grove City, Ohio. *Founded* 2020 Columbus, United States **$90M** last round Sept 2022 - 18 [**Ring Therapeutics** Ring Therapeutics is a biotechnology company based in Cambridge, Massachusetts, founded in 2017 by Flagship Pioneering.](https://millionrounds.com/company/ring-therapeutics) Ring Therapeutics is a biotechnology company based in Cambridge, Massachusetts, founded in 2017 by Flagship Pioneering. *Founded* 2017 Cambridge, United States **$87M** last round Mar 2023 - 19 [**GenSight Biologics** GenSight Biologics develops gene therapy-based treatments for retinal degenerative diseases.](https://millionrounds.com/company/gensight-biologics) GenSight Biologics develops gene therapy-based treatments for retinal degenerative diseases. *Founded* 2012 Paris, France **$80M** last round Mar 2026 - 20 [**XyloCor Therapeutics** XyloCor Therapeutics is a bio-pharmaceutical company intended to develop gene therapy for people with advanced coronary artery disease.](https://millionrounds.com/company/xylocor-therapeutics) XyloCor Therapeutics is a bio-pharmaceutical company intended to develop gene therapy for people with advanced coronary artery disease. *Founded* 2013 King of Prussia, United States **$68M** last round Feb 2025 - 21 [**Apertura Gene Therapy** Apertura Gene Therapy is a biotechnology company focused on developing advanced gene therapies for rare and genetic diseases.](https://millionrounds.com/company/apertura-gene-therapy) Apertura Gene Therapy is a biotechnology company focused on developing advanced gene therapies for rare and genetic diseases. *Founded* 2021 New York, United Kingdom **$67M** last round Apr 2022 - 22 [**Cyllene Therapeutics** EG 427, operating under the name Cyllene Therapeutics, is a biotechnology company based in Paris.](https://millionrounds.com/company/cyllene-therapeutics) EG 427, operating under the name Cyllene Therapeutics, is a biotechnology company based in Paris. *Founded* 2019 Paris, France **$66M** last round Jul 2026 - 23 [**Akamis Bio** Akamis Bio is a clinical-stage oncology company based in Cambridge, Massachusetts, dedicated to improving treatment for colorectal cancer and other solid tumors.](https://millionrounds.com/company/akamis-bio) Akamis Bio is a clinical-stage oncology company based in Cambridge, Massachusetts, dedicated to improving treatment for colorectal cancer and other solid tumors. *Founded* 2010 Cambridge, United Kingdom **$60M** last round Dec 2024 - 24 [**Myonexus Therapeutics** Myonexus Therapeutics is a clinical stage gene therapy company developing first ever treatments for Limb-girdle muscular dystrophy types.](https://millionrounds.com/company/myonexus-therapeutics) Myonexus Therapeutics is a clinical stage gene therapy company developing first ever treatments for Limb-girdle muscular dystrophy types. *Founded* 2017 Columbus **$60M** last round May 2018 - 25 [**Ixaka** Ixaka is a private cell and gene therapy company with a focus on the natural power of the body to cure disease.](https://millionrounds.com/company/ixaka) Ixaka is a private cell and gene therapy company with a focus on the natural power of the body to cure disease. *Founded* 2015 London **$54M** last round Jan 2021 - 26 [**Scout Bio** Scout Bi is a biotechnology company that specializes in veterinary, animal health, and gene therapy.](https://millionrounds.com/company/scout-bio) Scout Bi is a biotechnology company that specializes in veterinary, animal health, and gene therapy. *Founded* 2016 Philadelphia, United States **$53M** last round Oct 2021 - 27 [**Genespire** Genespire is a biotechnology company based in Milan, Italy, focused on developing innovative gene therapies for severe genetic diseases.](https://millionrounds.com/company/genespire) Genespire is a biotechnology company based in Milan, Italy, focused on developing innovative gene therapies for severe genetic diseases. *Founded* 2020 Milan, Italy **$52M** last round Sept 2024 - 28 [**NewBiologix** NewBiologix is a biotechnology and technology innovation company based in Epalinges, Switzerland, founded in 2022-2023.](https://millionrounds.com/company/newbiologix) NewBiologix is a biotechnology and technology innovation company based in Epalinges, Switzerland, founded in 2022-2023. *Founded* 2023 Epalinges, Switzerland **$50M** last round May 2023 - 29 [**Spot Biosystems** Spot Biosystems is building the next generation of non-viral gene therapy with an extracellular vesicle (EV) delivery platform.](https://millionrounds.com/company/spot-biosystems) Spot Biosystems is building the next generation of non-viral gene therapy with an extracellular vesicle (EV) delivery platform. *Founded* 2018 Palo Alto, United States **$40M** last round Jun 2026 - 30 [**Apic Bio** Apic Bio, Inc.](https://millionrounds.com/company/apic-bio) Apic Bio, Inc. *Founded* 2017 Cambridge, United States **$40M** last round Jan 2019 - 31 [**Opus Genetics** Opus Genetics is a gene therapy company for ultra-rare blinding conditions.](https://millionrounds.com/company/opus-genetics) Opus Genetics is a gene therapy company for ultra-rare blinding conditions. *Founded* 2004 Farmington Hills, United States **$35M** last round Apr 2026 - 32 [**Advanced Medicine Partners** Advanced Medicine Partners is a biotechnology company focused on process development, manufacturing, analytical development, and testing for advanced therapy pr](https://millionrounds.com/company/advanced-medicine-partners) Advanced Medicine Partners is a biotechnology company focused on process development, manufacturing, analytical development, and testing for advanced therapy pr *Founded* 2023 Cary, United States **$32M** last round Jun 2024 - 33 [**CoJourney** CoJourney is a global Contract Development and Manufacturing Organization (CDMO) focused on cell and gene therapy.](https://millionrounds.com/company/cojourney) CoJourney is a global Contract Development and Manufacturing Organization (CDMO) focused on cell and gene therapy. *Founded* 2021 Philadelphia, United States **$30M** last round Jun 2023 - 34 [**Genenta Science** Genenta Science is a biotechnology company that develops gene transfer therapy for the treatment of cancer tumors.](https://millionrounds.com/company/genenta-science) Genenta Science is a biotechnology company that develops gene transfer therapy for the treatment of cancer tumors. *Founded* 2014 Milano, Italy **$30M** last round Oct 2025 - 35 [**Newracle Genetics** Newracle Genetics is a bio venture company that develops gene therapy products for neurological diseases.](https://millionrounds.com/company/newracle-genetics) Newracle Genetics is a bio venture company that develops gene therapy products for neurological diseases. *Founded* 2018 Seoul **$27M** last round Jun 2021 - 36 [**Mana.bio** Mana.bio is an AI-based biotechnology startup founded in 2021, focused on enhancing targeted gene therapy delivery.](https://millionrounds.com/company/mana-bio) Mana.bio is an AI-based biotechnology startup founded in 2021, focused on enhancing targeted gene therapy delivery. *Founded* 2021 San Francisco, United States **$20M** last round Sept 2025 - 37 [**Celosia Therapeutics** A biotechnology company that uses gene therapy to treat neurodegenerative diseases.](https://millionrounds.com/company/celosia-therapeutics) A biotechnology company that uses gene therapy to treat neurodegenerative diseases. *Founded* 2022 Sydney, Australia **$17M** last round Nov 2024 - 38 [**Tozaro** Tozaro Limited is a UK-based biotechnology research company located in Colworth Park, Bedfordshire.](https://millionrounds.com/company/tozaro) Tozaro Limited is a UK-based biotechnology research company located in Colworth Park, Bedfordshire. *Founded* 2015 Bedford, United Kingdom **$16M** last round Feb 2026 - 39 [**StrideBio** StrideBio is a gene therapy company that develops genetic medicines with curative potential for patients with devastating conditions.](https://millionrounds.com/company/stridebio) StrideBio is a gene therapy company that develops genetic medicines with curative potential for patients with devastating conditions. *Founded* 2015 United States **$16M** last round Jun 2018 - 40 [**NeuExcell Therapeutics** NeuExcell Therapeutics is an early-stage gene therapy company focused on neurodegenerative diseases and central nervous system injuries.](https://millionrounds.com/company/neuexcell-therapeutics) NeuExcell Therapeutics is an early-stage gene therapy company focused on neurodegenerative diseases and central nervous system injuries. *Founded* 2016 King of Prussia, United States **$15M** last round May 2023 - 41 [**Celltrio** Celltrio is a life sciences company based in Fremont, California, specializing in automation solutions for cell culturing, biobanking, and cell and gene therapy.](https://millionrounds.com/company/celltrio) Celltrio is a life sciences company based in Fremont, California, specializing in automation solutions for cell culturing, biobanking, and cell and gene therapy. *Founded* 2018 Fremont, United States **$15M** last round Jun 2025 - 42 [**Calimmune** Calimmune is a clinical-stage gene therapy company.](https://millionrounds.com/company/calimmune) Calimmune is a clinical-stage gene therapy company. *Founded* 2006 United States **$15M** last round May 2015 - 43 [**Sino-Biocan** Sino-Biocan focuses on the research and development of domestic tools in the field of cell and gene therapy.](https://millionrounds.com/company/sino-biocan) Sino-Biocan focuses on the research and development of domestic tools in the field of cell and gene therapy. *Founded* 2013 Beijing **$14M** last round Mar 2024 - 44 [**Tongli Haiyuan Biotechnology** Tongli Haiyuan Biotechnology focuses on the R&D and production of GMP-grade core raw material reagents for upstream cell and gene therapy.](https://millionrounds.com/company/tongli-haiyuan-biotechnology) Tongli Haiyuan Biotechnology focuses on the R&D and production of GMP-grade core raw material reagents for upstream cell and gene therapy. *Founded* 2011 China **$13M** last round Mar 2023 - 45 [**ImmunoVec** ImmunoVec develops gene therapy treatments to cure terminal genetic diseases of the immune system.](https://millionrounds.com/company/immunovec) ImmunoVec develops gene therapy treatments to cure terminal genetic diseases of the immune system. *Founded* 2019 Santa Monica, United States **$13M** last round Jul 2026 - 46 [**AAVLife** Wildlife engages in developing gene therapy for the treatment of rare diseases.](https://millionrounds.com/company/aavlife) Wildlife engages in developing gene therapy for the treatment of rare diseases. *Founded* 2014 Paris, France **$12M** last round Apr 2014 - 47 [**Somagenetix** Somagenetix is a Swiss biotech company based in Zurich, specializing in gene therapy for phagocyte-related disorders and inherited genetic diseases.](https://millionrounds.com/company/somagenetix) Somagenetix is a Swiss biotech company based in Zurich, specializing in gene therapy for phagocyte-related disorders and inherited genetic diseases. *Founded* - Zuerich, Switzerland **$12M** last round Oct 2024 - 48 [**Genascence** Clinical-stage biotechnology company developing life-changing gene therapy products for musculoskeletal diseases](https://millionrounds.com/company/genascence) Clinical-stage biotechnology company developing life-changing gene therapy products for musculoskeletal diseases *Founded* 2017 Palo Alto, United States **$12M** last round Feb 2023 - 49 [**Autolomous** Autolomous is an biotechnology company engaged in manufacturing pragmatic digital solutions for cell and gene therapy.](https://millionrounds.com/company/autolomous) Autolomous is an biotechnology company engaged in manufacturing pragmatic digital solutions for cell and gene therapy. *Founded* 2019 London, United Kingdom **$11M** last round Mar 2025 - 50 [**Cardion** Cardion is a biopharmaceutical company that develops cardiovascular gene therapy products.](https://millionrounds.com/company/cardion) Cardion is a biopharmaceutical company that develops cardiovascular gene therapy products. *Founded* 1996 Germany **$11M** last round Sept 2002 **Total funding** how the list is ranked **15 November 2026** updated nightly **Rounds we track** source: Millionrounds Companies whose own description names this theme, ranked by the total they have raised in rounds we hold. Nobody pays to be on a list. ## Who backed them? Open any company for its rounds and investors, or search the investors who back gene therapy startups worldwide in the app, with filters, lists and exports. 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